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Last Close
15.30
Sep 04 • 3:59 PM ET Dollar change+0.45 Percentage change(3.03%)
Aftermarket Close
15.38
Aftermarket • 7:59 PM ET Dollar change+0.08 Percentage change(0.52%)
Sep 03, 9:45 AMUltragenyx Aspire Phase 3 apazunersen trial in Angelman syndrome fails, prompting multiple downgrades and target cuts including RBC to $19 from $40
Index
RUT
Market Cap
1.51B
Enterprise Value
2.42B
Income
-586.41M
Sales
716.93M
Book/sh
-2.96
Cash/sh
3.05
Dividend Est.
-
Dividend TTM
-
Dividend Ex-Date
-
Dividend Gr. 3/5Y
- -
Payout
-
Employees
1371
IPO
Jan 31, 2014
P/E
-
Forward P/E
-
PEG
-
P/S
2.10
P/B
-
P/C
5.01
P/FCF
-
EV/EBITDA
-
EV/Sales
3.37
Quick Ratio
1.56
Current Ratio
1.73
Debt/Eq
-
LT Debt/Eq
-
Option/Short
Yes / Yes
EPS (ttm)
-5.84
EPS next Y
-0.70
EPS next Q
-0.87
EPS this Y
31.44%
EPS next Y
82.48%
EPS next 5Y
71.02%
EPS past 3/5Y
16.78% -13.72%
Sales past 3/5Y
22.81% 19.95%
EPS Y/Y TTM
-5.66%
Sales Y/Y TTM
17.50%
EPS Q/Q
22.67%
Sales Q/Q
28.53%
Insider Own
8.80%
Insider Trans
-0.51%
Inst Own
105.48%
Inst Trans
1.00%
ROA
-45.63%
ROE
-656.54%
ROIC
-70.23%
Gross Margin
78.47%
Oper. Margin
-73.77%
Profit Margin
-81.79%
SMA20
-38.88%
SMA50
-44.79%
SMA200
-41.15%
Trades
Shs Outstand
98.30M
Shs Float
89.91M
52W High
39.89 -61.64%
52W Low
13.81 10.79%
Volatility
5.34% 4.77%
ATR (14)
2.05
RSI (14)
21.14
Beta
0.31
Rel Volume
4.09
Avg Volume
2.81M
Volume
11,494,472
Perf Week
-40.26%
Perf Month
-40.74%
Perf Quarter
-30.17%
Perf Half Y
-28.00%
Perf YTD
-33.48%
Perf Year
-51.09%
Perf 3Y
-59.50%
Perf 5Y
-85.06%
Perf 10Y
-76.51%
Prev Close
14.85
Price
15.30
Change %
3.03%
Date Action Analyst Rating Change Price Target Change
Sep-03-26Downgrade William Blair Outperform → Mkt Perform
Sep-03-26Downgrade Wells Fargo Overweight → Equal Weight $18
Sep-03-26Downgrade Robert W. Baird Outperform → Neutral $16
Sep-03-26Downgrade JP Morgan Overweight → Neutral $36
Sep-03-26Downgrade Evercore ISI Outperform → In-line $16
Sep-03-26Downgrade BofA Securities Buy → Neutral
Mar-24-26Downgrade Goldman Buy → Neutral $25
Oct-20-25Initiated Wells Fargo Overweight $65
Jul-28-25Resumed H.C. Wainwright Buy $80
May-28-25Initiated William Blair Outperform
Sep-04-26 03:24AM
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Ultragenyx Pharmaceutical, Inc. is a biopharmaceutical company, which engages in the identification, acquisition, development, and commercialization of novel products for the treatment of genetic diseases. Its products include Crysvita, Mepsevii, Dojolvi, and Evkeeza. The company was founded by Emil D. Kakkis in April 2010 and is headquartered in Novato, CA.
Ph.D.Dr. Emil D. Kakkis M.D.
Executive VP of Corporate Strategy & CFOMr. Howard Horn
Chief Legal Officer & Executive VP of Corporate AffairsMs. Karah Herdman Parschauer J.D.
Executive VP & Chief Commercial OfficerMr. Erik Harris M.B.A.
Chief Medical Officer & Executive VPDr. Eric Crombez M.D.
Insider Trading Relationship Date Transaction Cost #Shares Value ($) #Shares Total SEC Form 4
Parschauer Karah HerdmanEVP and Chief Legal OfficerAug 03 '26Sale24.921,90047,34892,562Aug 04 03:15 PM
Horn HowardChief Financial OfficerAug 03 '26Sale24.924,696117,02496,295Aug 04 03:13 PM
HOWARD HORNOfficerAug 03 '26Proposed Sale24.924,696117,024Aug 03 04:18 PM
Horn HowardChief Financial OfficerJul 01 '26Sale33.134,698155,645100,991Jul 06 03:37 PM
HOWARD HORNOfficerJul 01 '26Proposed Sale33.134,698155,645Jul 01 04:19 PM
Sanders Corazon (Corsee) D.DirectorJun 15 '26Sale25.052,00050,10021,095Jun 15 06:50 PM
Parschauer Karah HerdmanEVP and Chief Legal OfficerJun 15 '26Sale24.621,89946,75394,462Jun 15 06:46 PM
KARAH PARSCHAUEROfficerJun 15 '26Proposed Sale24.353,79992,506Jun 15 04:50 PM
CORAZON D. SANDERSDirectorJun 15 '26Proposed Sale25.052,00050,100Jun 15 04:12 PM
Horn HowardChief Financial OfficerJun 01 '26Sale23.774,653110,602105,689Jun 01 07:11 PM
HOWARD HORNOfficerJun 01 '26Proposed Sale23.774,653110,602Jun 01 04:08 PM
SULIMAN SHEHNAAZDirectorMay 18 '26Sale25.125,740144,18927,951May 18 06:41 PM
SHEHNAAZ SULIMANDirectorMay 18 '26Proposed Sale25.125,740144,189May 18 04:50 PM
Crombez EricEVP and Chief Medical OfficerMay 05 '26Sale24.963448,586111,189May 06 02:51 PM
Horn HowardChief Financial OfficerMay 01 '26Sale24.904,683116,607110,342May 04 05:35 PM
HOWARD HORNOfficerMay 01 '26Proposed Sale24.904,683116,607May 01 04:06 PM
Horn HowardChief Financial OfficerApr 01 '26Sale20.974,68398,20380,351Apr 02 06:19 PM
HOWARD HORNOfficerApr 01 '26Proposed Sale20.974,68398,203Apr 01 04:12 PM
Parschauer Karah HerdmanEVP and Chief Legal OfficerMar 06 '26Sale21.406,018128,78570,328Mar 10 04:51 PM
Parschauer Karah HerdmanEVP and Chief Legal OfficerMar 10 '26Sale22.673,50879,52666,820Mar 10 04:51 PM
KARAH PARSCHAUEROfficerMar 10 '26Proposed Sale22.673,50879,526Mar 10 04:42 PM
KARAH PARSCHAUEROfficerMar 06 '26Proposed Sale21.406,018128,775Mar 06 05:28 PM
Pinion John RichardSee RemarksMar 02 '26Sale22.8010,029228,661110,026Mar 03 07:09 PM
Harris ErikEVP & Chief Commercial OfficerMar 02 '26Sale22.8010,539240,28989,515Mar 03 07:08 PM
KAKKIS EMIL DPresident & CEOMar 02 '26Sale22.8054,4041,240,411658,994Mar 03 07:06 PM
Parschauer Karah HerdmanEVP and Chief Legal OfficerMar 02 '26Sale22.808,135185,47876,346Mar 03 06:51 PM
Huizenga Theodore AlanSVP, Chief Accounting OfficerMar 02 '26Sale22.801,63237,21048,670Mar 03 06:51 PM
Horn HowardChief Financial OfficerMar 02 '26Sale22.708,409190,91486,669Mar 03 06:50 PM
Horn HowardChief Financial OfficerMar 03 '26Sale22.401,63536,62485,034Mar 03 06:50 PM
Crombez EricEVP and Chief Medical OfficerMar 02 '26Sale22.807,029160,26176,301Mar 03 06:49 PM
HOWARD HORNOfficerMar 03 '26Proposed Sale22.401,63536,624Mar 03 04:41 PM
HOWARD HORNOfficerMar 02 '26Proposed Sale22.543,11970,302Mar 02 05:08 PM
Horn HowardChief Financial OfficerFeb 02 '26Sale23.563,06172,11788,935Feb 03 12:00 PM
HOWARD HORNOfficerFeb 02 '26Proposed Sale23.563,06172,117Feb 02 04:09 PM
Horn HowardChief Financial OfficerJan 02 '26Sale22.843,15071,94691,996Jan 05 04:07 PM
HOWARD HORNOfficerJan 02 '26Proposed Sale22.843,15071,946Jan 02 04:10 PM
Huizenga Theodore AlanSVP, Chief Accounting OfficerDec 29 '25Sale34.38852,92250,450Dec 30 01:49 PM
Horn HowardChief Financial OfficerDec 10 '25Sale36.383,081112,08795,146Dec 11 12:10 PM
HOWARD HORNOfficerDec 10 '25Proposed Sale36.383,081112,087Dec 10 04:05 PM
Horn HowardChief Financial OfficerOct 13 '25Sale31.517,942250,25298,227Oct 14 12:15 PM
Huizenga Theodore AlanSVP, Chief Accounting OfficerSep 18 '25Sale29.17641,86750,242Sep 19 06:23 PM
KARAH PARSCHAUEROfficerSep 12 '25Proposed Sale31.172,45076,366Sep 12 04:17 PM
Parschauer Karah HerdmanEVP and Chief Legal OfficerSep 12 '25Sale31.172,45076,36673,271Sep 12 04:11 PM